Risdiplam in Type 1 Spinal Muscular Atrophy

Baranello, Giovanni; Darras, Basil T.; Day, John W.; Deconinck, Nicolas; Klein, Andrea; Masson, Riccardo; Mercuri, Eugenio; Rose, Kristy; El-Khairi, Muna; Gerber, Marianne; Gorni, Ksenija; Khwaja, Omar; Kletzl, Heidemarie; Scalco, Renata S.; Seabrook, Timothy; Fontoura, Paulo; Servais, Laurent (2021). Risdiplam in Type 1 Spinal Muscular Atrophy. New England journal of medicine NEJM, 384(10), pp. 915-923. Massachusetts Medical Society MMS 10.1056/NEJMoa2009965

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Item Type:

Journal Article (Original Article)

Division/Institute:

04 Faculty of Medicine > Department of Gynaecology, Paediatrics and Endocrinology (DFKE) > Clinic of Paediatric Medicine > Neuropaediatrics
04 Faculty of Medicine > Department of Gynaecology, Paediatrics and Endocrinology (DFKE) > Clinic of Paediatric Medicine

UniBE Contributor:

Klein, Andrea Katharina

Subjects:

600 Technology > 610 Medicine & health

ISSN:

0028-4793

Publisher:

Massachusetts Medical Society MMS

Language:

English

Submitter:

Anette van Dorland

Date Deposited:

03 Mar 2022 16:03

Last Modified:

05 Dec 2022 16:08

Publisher DOI:

10.1056/NEJMoa2009965

PubMed ID:

33626251

BORIS DOI:

10.48350/165542

URI:

https://boris.unibe.ch/id/eprint/165542

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