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Relizani, Karima; Griffith, Graziella; Echevarría, Lucía; Zarrouki, Faouzi; Facchinetti, Patricia; Vaillend, Cyrille; Leumann, Christian; Garcia, Luis; Goyenvalle, Aurélie (2017). Efficacy and Safety Profile of Tricyclo-DNA Antisense Oligonucleotides in Duchenne Muscular Dystrophy Mouse Model. Molecular Therapy - Nucleic Acids, 8, pp. 144-157. Nature Publishing Group 10.1016/j.omtn.2017.06.013
Goyenvalle, Aurelie; Griffith, Graziella; Babbs, Arran; Andaloussi, Samir El; Ezzat, Kariem; Avril, Aurelie; Dugovic, Branislav; Chaussenot, Remi; Ferry, Arnaud; Voit, Thomas; Amthor, Helge; Bühr, Claudia; Schürch, Stefan; Wood, Matthew J. A.; Davies, Kay E.; Vaillend, Cyrille; Leumann, Christian; Garcia, Luis (2015). Functional correction in mouse models of muscular dystrophy using exon-skipping tricyclo-DNA oligomers. Nature medicine, 21(3), pp. 270-275. Nature Publishing Group 10.1038/nm.3765