Crowley, Suzanne; Azevedo, Inês; Boon, Mieke; Bush, Andrew; Eber, Ernst; Haarman, Eric; Karadag, Bulent; Kötz, Karsten; Leigh, Margaret; Moreno-Galdó, Antonio; Mussaffi, Huda; Nielsen, Kim G; Omran, Heymut; Papon, Jean-François; Pohunek, Petr; Priftis, Kostas; Rindlisbacher, Bernhard; Santamaria, Francesca; Valiulis, Arunas; Witt, Michal; ... (2020). Access to medicines for rare diseases: beating the drum for primary ciliary dyskinesia [editorial]. ERJ Open Research, 6(3), 00377-2020. European Respiratory Society 10.1183/23120541.00377-2020
|
Text
Crowley ERJOpenRes 2020.pdf - Published Version Available under License Creative Commons: Attribution-Noncommercial (CC-BY-NC). Download (626kB) | Preview |
Primary ciliary dyskinesia, a rare disease causing bronchiectasis, lacks a sound evidence base for treatment. @beatpcd proposes 1) forming a PCD European clinical trial network to address this situation and 2) conducting n-of-1 trials to access medication. https://bit.ly/3j5blfM.
Item Type: |
Journal Article (Further Contribution) |
|---|---|
Division/Institute: |
04 Faculty of Medicine > Department of Gynaecology, Paediatrics and Endocrinology (DFKE) > Clinic of Paediatric Medicine 04 Faculty of Medicine > Pre-clinic Human Medicine > Institute of Social and Preventive Medicine (ISPM) 04 Faculty of Medicine > Department of Gynaecology, Paediatrics and Endocrinology (DFKE) > Clinic of Paediatric Medicine > Paediatric Pneumology |
UniBE Contributor: |
Kühni, Claudia |
Subjects: |
600 Technology > 610 Medicine & health 300 Social sciences, sociology & anthropology > 360 Social problems & social services |
ISSN: |
2312-0541 |
Publisher: |
European Respiratory Society |
Funders: |
[4] Swiss National Science Foundation |
Language: |
English |
Submitter: |
Anette van Dorland |
Date Deposited: |
15 Oct 2020 20:01 |
Last Modified: |
05 Dec 2022 15:40 |
Publisher DOI: |
10.1183/23120541.00377-2020 |
PubMed ID: |
32964005 |
BORIS DOI: |
10.7892/boris.146860 |
URI: |
https://boris.unibe.ch/id/eprint/146860 |
Actions (login required)
 |
Edit item |